The firm at the JP Morgan Healthcare Conference additionally expects a regulatory decision on its gene therapy RGX-121 for Hunter syndrome next month.

Sarepta Therapeutics, Inc. (NASDAQ:SRPT), the leader in precision genetic medicine for rare diseases, today reports ...

Scientists at Duke-NUS Medical School have uncovered how exercise helps aging muscles regain their ability to repair ...

The FDA granted fast track status to VectorY’s VTx-002, an antibody gene therapy targeting TDP-43 protein aggregates in ALS.

A new study suggests that a little-known region deep in the brain could be crucial for preserving physical strength as we age ...

The lymphatic system is a network of lymphoid organs and lymphatic vessels. It transports lymph fluid and helps to clear toxins and other waste from the body’s tissues. Lymphocytes use the lymphatic ...