Spinal muscular atrophy (SMA) is a severe, inherited, progressive neuromuscular disease that causes devastating muscle atrophy and disease-related complications. It is the most common genetic cause of ...
3don MSN
Boy, 5, Born with Rare Genetic Disorder Walks by Himself After Receiving World’s Most Expensive Drug
Megan Willis' son, Edward, was given the gene therapy, Zolgensma, after being diagnosed with spinal muscular atrophy when he ...
—The slow progression of SMA in adults and older children complicates evaluation of treatment response to newer therapies. Longitudinal quantitative MRI (qMRI) may give clinicians a better handle on ...
A five-year-old boy who received the world's most expensive drug as a baby has made "incredible progress" and can walk ...
Spinal muscular atrophy (SMA) is a genetic neuromuscular disease affecting specialized nerve cells that control voluntary muscle movement, according to the Muscular Dystrophy Association (MDA). It can ...
The loss of muscle mass with increased fat mass in patients with SMA suggests a dietary imbalance between energy intake and expenditure. Dietary modifications have shown some promise in managing SMA, ...
Join the community workshop in Thiruvananthapuram to support families affected by Spinal Muscular Atrophy and learn about the condition.
DUBLIN--(BUSINESS WIRE)--The "Spinal Muscular Atrophy (SMA) - Pipeline Review, H2 2020" drug pipelines has been added to ResearchAndMarkets.com's offering. Spinal Muscular Atrophy - Pipeline Review, ...
Peter L. Salgo, MD: Now we’re going to look at something called spinal muscular atrophy [SMA]. I must tell you that before researching it for this broadcast, it was not a disease that was on my radar.
The MarketWatch News Department was not involved in the creation of this content. SCHAUMBURG, Ill., Nov. 26, 2025 /PRNewswire/ -- Cure SMA, the leading nonprofit organization dedicated to supporting ...
Spinal muscular atrophy (SMA) and spina bifida are distinct conditions that affect the nerves that allow for voluntary motor control. Share on Pinterest press coverage photography/Getty Images SMA is ...
Nicholas' mother was a friend of mine from my hometown across the state. Our families had been friends for as long as I can remember. She and I were pregnant at the same time, even taking our giant, ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback